eRAM
encyclopedia of Rare Disease Annotation for Precision Medicine
| Disease | cystic fibrosis |
| Symptom | C0030286|pancreatic disease |
| Sentences | 1 |
| PubMedID- 24257348 | Gene therapy offers the possibility to treat pancreatic disease in cystic fibrosis (cf), caused by mutations in the cf transmembrane conductance regulator (cftr) gene; however, gene transfer to the pancreas is untested in humans. |
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